Agios Pharma' PYRUKYND approved in the European Union for adults with Thalassemia
[출처/시간] Briefing.com - 9:16 AM ET, 05/22/2026 PYRUKYND is the only medicine approved in the EU for adults with transfusion-dependent and non-transfusion-dependent alpha- or beta-thalassemia.Mitapivat is now approved for thalassemia in the U.S., Saudi Arabia, United Arab Emirates, and EU.Avanzanite Bioscience B.V., a specialty pharmaceutical company, will continue to distribute and commercialize PYRUKYND in Europe.
[출처/시간] Briefing.com - 9:16 AM ET, 05/22/2026
PYRUKYND is the only medicine approved in the EU for adults with transfusion-dependent and non-transfusion-dependent alpha- or beta-thalassemia.Mitapivat is now approved for thalassemia in the U.S., Saudi Arabia, United Arab Emirates, and EU.Avanzanite Bioscience B.V., a specialty pharmaceutical company, will continue to distribute and commercialize PYRUKYND in Europe.
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